Tag Archives: Disease

FDA grants Jacobus Pharma approval for rare disease drug

(Reuters) – Jacobus Pharmaceutical Co Inc on Monday won U.S. approval for the first drug to treat children with Lambert-Eaton myasthenic syndrome, a rare autoimmune disorder. The drug, Ruzurgi, was approved for use in patients aged between 6 and 17, the FDA said here. Lambert-Eaton myasthenic syndrome, which affects about three people per million worldwide,… Read More »

Protein protects against non-alcoholic fatty liver disease

Researchers propose a possible therapeutic target to treat fatty liver, a disease for which there is currently no treatment. Non-alcoholic fatty liver disease describes several liver dysfunctions of varying severity, characterised by the accumulation of fat in hepatic cells and not caused by high alcohol consumption. This disease, one of the most common in developed… Read More »

Patients’ own cells could be the key to treating Crohn’s disease

Rachel Sawyer, a communications manager who is 50 and lives in Anerley in south east London, was diagnosed with Crohn’s disease in 2000 and treated at Guy’s and St Thomas’. Although her condition is now under control, she supports other people who have Crohn’s and runs the Twitter account @Bottomline_IBD. She said: “One of the worst… Read More »